机译:基因疗法可挽救狗的感光细胞失明,为治疗人类X连锁性色素性视网膜炎铺平道路
Section of Ophthalmology, School of Veterinary Medicine, University of Pennsylvania, Philadelphia, PA 19104;
Department of Ophthalmology, Scheie Eye Institute, University of Pennsylvania Perelman School of Medicine, Philadelphia, PA 19104;
Department of Molecular Genetics and Microbiology, University of Florida, Gainesville, FL 32610;
Section of Ophthalmology, School of Veterinary Medicine, University of Pennsylvania, Philadelphia, PA 19104;
Department of Ophthalmology and Visual Sciences, University of Michigan, Ann Arbor, Ml 48105;
Department of Ophthalmology, Scheie Eye Institute, University of Pennsylvania Perelman School of Medicine, Philadelphia, PA 19104;
Department of Ophthalmology, University of Florida, Gainesville, FL 32610;
Department of Molecular Genetics and Microbiology, University of Florida, Gainesville, FL 32610;
Department of Ophthalmology and Visual Sciences, University of Michigan, Ann Arbor, Ml 48105;
Department of Ophthalmology, University of Florida, Gainesville, FL 32610;
Department of Ophthalmology, Scheie Eye Institute, University of Pennsylvania Perelman School of Medicine, Philadelphia, PA 19104;
Department of Ophthalmology, Scheie Eye Institute, University of Pennsylvania Perelman School of Medicine, Philadelphia, PA 19104;
Department of Ophthalmology, University of Florida, Gainesville, FL 32610;
Section of Ophthalmology, School of Veterinary Medicine, University of Pennsylvania, Philadelphia, PA 19104;
Department of Ophthalmology and Visual Sciences, University of Michigan, Ann Arbor, Ml 48105,Neurobiology-Neurodegeneration and Repair Laboratory, National Eye Institute, National Institutes of Health, Bethesda, MD 20892;
Department of Ophthalmology, University of Florida, Gainesville, FL 32610;
Department of Ophthalmology, Scheie Eye Institute, University of Pennsylvania Perelman School of Medicine, Philadelphia, PA 19104;
Section of Ophthalmology, School of Veterinary Medicine, University of Pennsylvania, Philadelphia, PA 19104;
机译:X连锁性视网膜色素变性鼠模型中的人类RPGR缩写基因对感光器的抢救
机译:由GRK1启动子驱动的两个AAV2 / 5介导的RPGR基因扩增构建物在RPGR X连锁性色素性视网膜色素变性的犬模型中挽救了感光细胞的结构和功能
机译:由GRK1启动子驱动的两个AAV2 / 5介导的RPGR基因扩增构建物在RPGR X连锁性色素性视网膜色素变性的犬模型中挽救了感光细胞的结构和功能
机译:用相敏AO-OCT测量色素性视网膜炎中视锥细胞感光功能障碍
机译:色素性视网膜炎动物模型中光感受器变性的生长因子抢救。
机译:基因疗法可挽救狗的感光细胞失明为治疗人类X连锁性色素性视网膜炎铺平道路
机译:对人类致盲性疾病的洞察♦:由于P23H视蛋白突变导致的常染色体显性遗传性视网膜色素变性的常见形式的新小鼠模型中光感受器变性的探测机制