首页>
外国专利>
RP2 AND RPGR VECTORS FOR TREATING X-LINKED RETINITIS PIGMENTOSA
RP2 AND RPGR VECTORS FOR TREATING X-LINKED RETINITIS PIGMENTOSA
展开▼
机译:RP2和RPGR矢量治疗X链接的视网膜色素沉着症
展开▼
页面导航
摘要
著录项
相似文献
摘要
Disclosed are adeno-associated virus (AAV) vectors comprising a nucleotide sequence encoding RP2 or RPGR-ORF15 and related pharmaceutical compositions. Also disclosed are methods of treating or preventing X-linked retinitis pigmentosa, increasing photoreceptor number in a retina of a mammal, and increasing visual acuity of a mammal using the vectors and pharmaceutical compositions.
展开▼