A method for performing antisense oligonucleotide-mediated exon skipping in the retina of a subject in need of it.

摘要

PROBLEM TO BE SOLVED: To provide a method for performing antisense oligonucleotide-mediated exon skipping in the retina of a subject in need thereof. SOLUTION: The method includes a step of injecting a certain amount of antisense oligonucleotide into the intravitreal body of a target. [Selection diagram] None