PHARMACEUTICAL COMPOSITION COMPRISING FUSION PROTEIN OF CELL-PENETRATING PEPTIDE AND RPE65 FOR TREATMENT OF LEBER'S CONGENITAL AMAUROSIS

摘要

The present disclosure relates to a composition including a conjugate of a cell-penetrating peptide and RPE65 (Retinal Pigment Epithelium-specific 65 kDa) as an active ingredient. The composition may be useful for the treatment of Leber's congenital amaurosis because RPE65 has increased cell permeability.